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What Is Clicinal Trial?
A clinical trial is a human research study that aims to answer specific questions concerning novel medicines, vaccinations, diagnostic techniques, or new methods of using existing treatments. Clinical trials are used to test the safety and efficacy of novel medications, diagnostics, and therapies.
Because of factors such as well-established medical infrastructure, quick clearance deadlines, an agile regulatory system, generally acknowledged clinical trial data, and many more, the United States has continuously emerged as a prominent venue for clinical research. International clinical trials provide several options. Our clinical trial teams may work together worldwide to provide more effective treatment and get more comprehensive findings.
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How does it works?
Clinical trial patient from India.
Recently, an 8-year-old male patient from India was matched for the clinical trial for a rare kind of genetic disease known as Duchenne Muscular Dystrophy (DMD). The patient was matched for the MIS510N trail program and gene therapy program.
What is Duchenne Muscular Dystrophy?
Duchenne muscular dystrophy is a genetic condition that results in progressive muscle weakness and wasting. A mutation in the gene that encodes for the protein dystrophin, which is required for muscle function, causes it. Duchenne muscular dystrophy primarily affects boys, with symptoms typically manifesting in childhood. Children with the disorder may struggle to walk and develop a distinctive waddling gait. Fatigue, difficulty breathing, and scoliosis are some of the other symptoms.The condition is associated with the most severe clinical symptoms of all the Muscular dystrophies. DMD is caused due to the genetic mutation on one of the mother’s X chromosomes and the researchers have found some of the affected genes.
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